Forschungsdatenbank

Forschungsprojekt
Projektleiter:   Univ.-Prof. Dr. Julia B Hennermann, Dr. Eugen Mengel

EFC14028-COMET mit Substanz GZ402666-neoGAA

A phase 3 randomized, multicenter, multinational, double blinded study comparing the efficacy and safety of repeated biweekly infusions of neoGAA (GZ402666) and alglucosidase alfa in treatment naive patients with late onset Pompe disease
 
Laufzeit:  2018-2020